Anthony Saleh
Chief Executive Officer miRecule
Seminars
Thursday 29th January 2026
Expanding RNAi Delivery to Muscle Tissue Through Antibody Oligonucleotide Conjugates
12:00 pm
- Antibody-siRNA conjugates enable muscle-selective uptake, treating myopathies with minimal off-target effects
- Enhanced endosomal escape increases cytoplasmic siRNA release, improving dystrophin restoration in Duchenne MD
- Modular platform allows rapid re-targeting, accelerating therapies for multiple rare muscle disorders
