Workshop A: Resolving the Challenge of Targeting Beyond the Liver: Understanding How the Field is Targeting the CNS, Skin & Eyes to Unlock the Potential of RNAi Therapeutics
Time: 9:00 am
day: Pre-Conference Day
Details:
Recent advancements have been made in targeting outside of the liver, this includes targeting the CNS, skin and eyes. Therefore, in order to continue the success of RNAi-based therapeutics, it is important to understand the vital parameters to allow for delivery to currently undruggable targets.
This workshop will gather experts to discuss:
• Understanding how to cross the BBB and utilizing this to successfully design a delivery platform
• How is the field approaching the challenges of crossing the BBB?
• What are the new delivery platforms which have been developed to target the skin?
• What are important safety parameters to consider when targeting or treating retinal diseases and related detection methods?
• How to establish siRNA-based target validation and develop therapeutic platforms for retinal diseases?
