Leveraging a Novel RNAi Delivery Platform and Strategy for Extrahepatic Targeted Therapy
- Exploiting a novel RNAi delivery modality due to unique uptake and release kinetics for the development of acute RNAi therapeutics
- Leveraging direct tissue targeting of RNAi therapeutics to unlock previously inaccessible conditions for improved therapeutic outcomes
- Using selective translational models to derisk RNAi therapeutic development for pipeline acceleration