Extended Nucleic Acid (exNA): A Platform Technology for Enhancing siRNA Efficacy & Tissue Accumulation In Vitro
Time: 1:30 pm
day: Conference Day One
Details:
• Metabolic stabilization of siRNA backbone for longer duration of effect in vivo
• Significantly improved oligonucleotide plasma PK profile
• The improved potency and durability open extrahepatic tissues and indications to therapeutic interventions