Extended Nucleic Acid (exNA): A Platform Technology for Enhancing siRNA Efficacy & Tissue Accumulation In Vitro

Time: 1:30 pm
day: Conference Day One

Details:

• Metabolic stabilization of siRNA backbone for longer duration of effect in vivo

• Significantly improved oligonucleotide plasma PK profile

• The improved potency and durability open extrahepatic tissues and indications to therapeutic interventions 

Speakers: