Expanding RNAi Delivery to Muscle Tissue Through Antibody Oligonucleotide Conjugates
- Antibody-siRNA conjugates enable muscle-selective uptake, treating myopathies with minimal off-target effects
- Enhanced endosomal escape increases cytoplasmic siRNA release, improving dystrophin restoration in Duchenne MD
- Modular platform allows rapid re-targeting, accelerating therapies for multiple rare muscle disorders