RNAi 2.0: Massively Parallel Functional Platforms De-Risk & Accelerate R&D

Time: 3:30 pm
day: Day Two


  • Quantitative functional screens identify single-digit pico-molar hits and optimize PK properties
  • Fit-for-purpose synthetic biology systems validate leads and teach the rational design prediction engine
  • Extra-hepatic targeting, using prophylactic and/or treatment regimens are becoming a reality